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Contrassegna composito Scommessa crim negative pompe osso vincoli compagno

Immunological challenges and approaches to immunomodulation in Pompe  disease: a literature review. - Abstract - Europe PMC
Immunological challenges and approaches to immunomodulation in Pompe disease: a literature review. - Abstract - Europe PMC

A new assay for fast, reliable CRIM status determination in infantile-onset  Pompe disease - ScienceDirect
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect

Transforming the clinical outcome in CRIM-negative infantile Pompe disease  identified via newborn screening: the benefits of early treatment with  enzyme replacement therapy and immune tolerance induction | Genetics in  Medicine
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine

A new assay for fast, reliable CRIM status determination in infantile-onset  Pompe disease - ScienceDirect
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect

Child Neurology: Pompe disease | Neurology
Child Neurology: Pompe disease | Neurology

CRIM-negative infantile Pompe disease: characterization of immune responses  in patients treated with ERT monotherapy - ScienceDirect
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy - ScienceDirect

PDF) Successful Immune Tolerance Induction to Enzyme Replacement Therapy in  CRIM-Negative Infantile Pompe Disease
PDF) Successful Immune Tolerance Induction to Enzyme Replacement Therapy in CRIM-Negative Infantile Pompe Disease

Children | Free Full-Text | The Clinical Management of Pompe Disease: A  Pediatric Perspective
Children | Free Full-Text | The Clinical Management of Pompe Disease: A Pediatric Perspective

The impact of antibodies on clinical outcomes in diseases treated with  therapeutic protein: Lessons learned from infantile Pompe disease |  Genetics in Medicine
The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: Lessons learned from infantile Pompe disease | Genetics in Medicine

Efficacy of ERT+ITI in CRIM-negative IPD patients treated in the... |  Download Table
Efficacy of ERT+ITI in CRIM-negative IPD patients treated in the... | Download Table

Algorithm for the Early Diagnosis and Treatment of Patients with Cross  Reactive Immunologic Material- Negative Classic Infantile
Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material- Negative Classic Infantile

Frontiers | Recommendations for Infantile-Onset and Late-Onset Pompe  Disease: An Iranian Consensus
Frontiers | Recommendations for Infantile-Onset and Late-Onset Pompe Disease: An Iranian Consensus

Transforming the clinical outcome in CRIM-negative infantile Pompe disease  identified via newborn screening: the benefits of early treatment with  enzyme replacement therapy and immune tolerance induction | Genetics in  Medicine
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine

JCI Insight - Sustained immune tolerance induction in enzyme replacement  therapy–treated CRIM-negative patients with infantile Pompe disease
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease

JCI Insight - Sustained immune tolerance induction in enzyme replacement  therapy–treated CRIM-negative patients with infantile Pompe disease
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease

Enzyme therapy and immune response in relation to CRIM status: the Dutch  experience in classic infantile Pompe disease | Journal of Inherited  Metabolic Disease
Enzyme therapy and immune response in relation to CRIM status: the Dutch experience in classic infantile Pompe disease | Journal of Inherited Metabolic Disease

Early ERT Key in Severe Classic Infantile Pompe, Study Finds
Early ERT Key in Severe Classic Infantile Pompe, Study Finds

Treatment approach for IOPD. CRIM, cross-reactive immunologic... | Download  Scientific Diagram
Treatment approach for IOPD. CRIM, cross-reactive immunologic... | Download Scientific Diagram

JCI Insight - Sustained immune tolerance induction in enzyme replacement  therapy–treated CRIM-negative patients with infantile Pompe disease
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease

Targeted approaches to induce immune tolerance for Pompe disease therapy:  Molecular Therapy Methods & Clinical Development
Targeted approaches to induce immune tolerance for Pompe disease therapy: Molecular Therapy Methods & Clinical Development

Transforming the clinical outcome in CRIM-negative infantile Pompe disease  identified via newborn screening: the benefits of early treatment with  enzyme replacement therapy and immune tolerance induction - ScienceDirect
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction - ScienceDirect

CRIM-negative infantile Pompe disease: characterization of immune responses  in patients treated with ERT monotherapy | Genetics in Medicine
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy | Genetics in Medicine

Characterization of immune response in Cross-Reactive Immunological  Material (CRIM)-positive infantile Pompe disease patients treated with  enzyme replacement therapy - ScienceDirect
Characterization of immune response in Cross-Reactive Immunological Material (CRIM)-positive infantile Pompe disease patients treated with enzyme replacement therapy - ScienceDirect

A new assay for fast, reliable CRIM status determination in infantile-onset  Pompe disease - ScienceDirect
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect

Sustained immune tolerance induction in enzyme replacement therapy–treated  CRIM-negative patients with infantile Pompe disease
Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease

A new assay for fast, reliable CRIM status determination in infantile-onset  Pompe disease - ScienceDirect
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect

Pompe Disease
Pompe Disease

Frontiers | A Race Against Time—Changing the Natural History of CRIM  Negative Infantile Pompe Disease
Frontiers | A Race Against Time—Changing the Natural History of CRIM Negative Infantile Pompe Disease

Transforming the clinical outcome in CRIM-negative infantile Pompe disease  identified via newborn screening: the benefits of early treatment with  enzyme replacement therapy and immune tolerance induction | Genetics in  Medicine
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine